Nusinersen - an overview | ScienceDirect Topics
Biomolecules | Free Full-Text | Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy
Mechanism of action of nusinersen | Download Scientific Diagram
Mechanism of approved therapeutics. (A) Nusinersen regulates splicing... | Download Scientific Diagram
Frontiers | History of development of the life-saving drug “Nusinersen” in spinal muscular atrophy
Antisense oligonucleotides (ASOs) in clinical use. (A) Nusinersen binds... | Download Scientific Diagram
SPINRAZA (nusinersen) injection, for intrathecal use
nusinersen | Ligand page | IUPHAR/BPS Guide to PHARMACOLOGY
Advances in oligonucleotide drug delivery | Nature Reviews Drug Discovery
Nusinersen - Wikipedia
Targeting the 5′ untranslated region of SMN2 as a therapeutic strategy for spinal muscular atrophy: Molecular Therapy - Nucleic Acids
Quality of Life in SMA Patients Under Treatment With Nusinersen
Frontiers | History of development of the life-saving drug “Nusinersen” in spinal muscular atrophy
Nusinersen ameliorates motor function and prevents motoneuron Cajal body disassembly and abnormal poly(A) RNA distribution in a SMA mouse model | Scientific Reports
IJMS | Free Full-Text | High Concentration of an ISS-N1-Targeting Antisense Oligonucleotide Causes Massive Perturbation of the Transcriptome
FN170919 | 1258984-36-9 | Nusinersen | Biosynth
Cut and Paste: Treating Spinal Muscular Atrophy with Nusinersen - YouTube
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study - The Lancet
Combined treatment with the histone deacetylase inhibitor LBH589 and a splice‐switch antisense oligonucleotide enhances SMN2 splicing and SMN expression in Spinal Muscular Atrophy cells - Pagliarini - 2020 - Journal of Neurochemistry -
Spinraza, INN - nusinersen
Biomolecules | Free Full-Text | Nusinersen Induces Disease-Severity-Specific Neurometabolic Effects in Spinal Muscular Atrophy
Nusinersen (Spinraza®) – Spinal Muscular Atrophy (SMA) | National Institute of Neurological Disorders and Stroke
Spinraza (Nusinersen) for SMA | SMA News Today
Discovery of a CNS penetrant small molecule SMN2 splicing modulator with improved tolerability for spinal muscular atrophy | Scientific Reports
